The avalglucosidase alfa phase 3 COMET trial in late-onset Pompe disease patients: Efficacy and safety results after 97 weeks
Authors
Priya Kishnani ; Jordi Díaz-Manera ; Hani Kushlaf ; Shafeeq Ladha ; Tahseen Mozaffar ; Volker Straub b ; Antonio Toscano ; Ans T. van der Ploeg ; Kenneth I. Berger ; Paula R. Clemens j, Yin-Hsiu Chien ; John W. Day ; Sergey Illarioshkin ; Mark Roberts ; Shahram Attarian ; Gerson Carvalho ; Young-Chul Choi ; Sevim Erdem-Özdamar ; Ozlem Goker-Alpan ; Anna Kostera-Pruszczyk ; Kristina An Haack ; Nathan Thibault ; Tianyue Zhou ; Mazen M. Dimachkie ; Benedikt Schoser
Citation
MOLECULAR GENETICS AND METABOLISM, Vol.135(2) : S66-S67, 2022-02