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| MSYSTEMS |
| 2025 | Recent preclinical and clinical advances in gene therapy for hereditary hearing loss
| MOLECULES AND CELLS |
| 2025 | Engineered virus-like particles for in vivo gene editing ameliorate hearing loss in murine DFNA2 model | MOLECULAR THERAPY |
| 2025 | Antisense oligonucleotide therapy mitigates autosomal dominant progressive hearing loss in a murine model of human DFNA2
| MOLECULAR THERAPY |
| 2025 | Type I interferon signaling promotes kainic acid-induced seizures through mTOR activation | NEUROPHARMACOLOGY |
| 2025 | Autophagy inhibition enhances sensitivity of alpelisib in PI3K–mutated non-small cell lung cancer | BIOMEDICINE & PHARMACOTHERAPY |
| 2025 | Condensation of the Golgi Apparatus Activates YAP1 to Promote Gastric Cancer Progression | CANCER RESEARCH |
| 2025 | Beyond the Secretory Pathway: New Insights Into Protein Release
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| 2025 | Comprehensive resistance profiling of chronic myeloid leukaemia associated ABL1 variants against five tyrosine kinase inhibitors using prime editing | NATURE BIOMEDICAL ENGINEERING |
| 2025 | Functional Testing of Human Disease Missense Variants in Caenorhabditis elegans by Targeting COQ2 Variants
| KIDNEY INTERNATIONAL REPORTS |
| 2025 | High-throughput evaluation of in vitro CRISPR activities enables optimized large-scale multiplex enrichment of rare variants | NATURE BIOMEDICAL ENGINEERING |
| 2025 | Short-term memory errors are strongly associated with a drift in neural activity in the posterior parietal cortex
| PLOS BIOLOGY |
| 2025 | ER tubular body: an ER-derived compartment for redirecting autophagy to secretory functions | AUTOPHAGY |
| 2025 | The elucidation of the dual role of Beclin-1 in ischemic stroke through systems biology modeling
| ISCIENCE |
| 2025 | Functional assessment of all ATM SNVs using prime editing and deep learning | CELL |
| 2025 | Saturation profiling of drug-resistant genetic variants using prime editing | NATURE BIOTECHNOLOGY |
| 2025 | Application of population pharmacokinetic modeling of SVG-101 to evaluate proper dose selection
| Translational and Clinical Pharmacology |
| 2025 | Leveraging underrepresented population data improves interpretation of genetic variants associated with hearing loss
| SCIENTIFIC REPORTS |
| 2025 | Safety and Anti-Inflammatory Effects of Engineered Extracellular Vesicles (ILB-202) for NF-κB Inhibition: A Double-Blind, Randomized, Placebo-Controlled Phase 1 Trial
| JOURNAL OF EXTRACELLULAR VESICLES |
| 2025 | Evaluation and prediction of guide RNA activities in genome-editing tools | NATURE REVIEWS BIOENGINEERING |