Browsing "1. Journal Papers" by Other Title : Jordi Diaz-Manera ; Priya S Kishnani ; Hani Kushlaf ; Shafeeq Ladha ; Tahseen Mozaffar ; Volker Straub ; Antonio Toscano ; Ans T van der Ploeg ; Kenneth I Berger ; Paula R Clemens ; Yin-Hsiu Chien ; John W Day ; Sergey Illarioshkin ; Mark Roberts ; Shahram Attarian ; Joao Lindolfo Borges ; Francoise Bouhour ; Young Chul Choi ; Sevim Erdem-Ozdamar ; Ozlem Goker-Alpan ; Anna Kostera-Pruszczyk ; Kristina An Haack ; Christopher Hug ; Olivier Huynh-Ba ; Judith Johnson ; Nathan Thibault ; Tianyue Zhou ; Mazen M Dimachkie ; Benedikt Schoser ; COMET Investigator Group

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Issue DateTitleJournal Title
2021Safety and efficacy of avalglucosidase alfa versus alglucosidase alfa in patients with late-onset Pompe disease (COMET): a phase 3, randomised, multicentre trialLANCET NEUROLOGY
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